GENE THERAPY

 GENE  THERAPY 

Gene therapy is an innovative approach to treating various diseases by the delivery of functional genes into the cells to replace missing or defective genes.Gene therapy has the potential to offer a cure for a range of conditions that are caused by genetic mutations or disorders.

Gene therapy involves the delivery of therapeutic or working genes into a patient's cells.

There are 2 ways to deliver gene therapy to address gene mutations: outside the body, known as ex vivo, or inside the body, known as in vivo.

Ex vivo means gene therapy is added to your cells OUTSIDE of your body.

In this process:

Certain cells are removed from your body and taken to a lab

Scientists make changes to the genes inside of the cells

These changes treat or correct mutations

Cells are then returned to your body

In vivo means that gene therapy is given straight to your cells INSIDE your body.

In this process:

Gene therapy is typically administered through an IV

Cells are edited inside the body

Both ex vivo and in vivo methods require a delivery vehicle, or vector, to get the treatment into the cell.

Gene therapy isn’t a new idea. The Food and Drug Administration (FDA) has approved several gene therapies, and there are more being researched. The future of medicine is full There are 2 ways to deliver gene therapy to address gene mutations: outside the body, known as ex vivo, or inside the body, known as in vivo.

What Can Gene Therapy Treat?

Gene therapy has the potential to treat a wide range of conditions.Gene therapy introduces functional genes into the patient's cells to replace the missing or defective genes.

1. Inherited Genetic Disorder: 

These are diseases caused by mutations in an individual's genes, that result in the production of non-functional or absent proteins.

2. Cancer: 

Cancer cells often have mutations in their DNA that cause them to grow and divide uncontrollably, therapy introduces therapeutic genes into the cancer cells to stop their uncontrolled growth and division.

3. Neurological Disorder: 

Diseases that affect the nervous system, including conditions such as ;